Before and After Gene Therapy

Rylae-Ann was born in 2018 with AADC Deficiency, debilitating disease. If they are fortunate to live past 4 years old, they will require a lifetime of care. When she was 18 months old, she had gene therapy in November 2019. She has now lived most of her life post-gene therapy. The results have been life-changing and miraculous. We continue to push her to achieve all that she can.