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MS 试验结果表明药物可以修复损伤
1 month ago
3
突破性发现!两种常见药物或能修复多发性硬化症损伤,为患者带来新希望。
早期试验显示,糖尿病药物和抗组胺药可能修复多发性硬化症中受损的髓鞘——神经的保护层。剑桥大学领导的这项研究被多发性硬化症协会称为“真正令人兴奋”的进展,或为阻止疾病发展迈出关键一步,但仍需验证长期效果与安全性。
试验负责人尼克·康尼夫博士表示:“十年内,我们或迎来首款修复髓鞘的许可疗法,改善患者生活。”但他强调,仍需验证长期效果与副作用。“但直觉告诉我,我们正接近阻止病情恶化的新疗法。”
多发性硬化症会引发免疫系统攻击髓鞘,导致疲劳、行走困难等症状。英国现有超15万患者,每周新增135例。现有疗法仅针对免疫系统,无法阻止神经损伤。
试验中,半数患者接受药物治疗,另一半使用安慰剂。六个月后,药物组神经信号传递速度保持稳定,而安慰剂组减慢。参与者安娜贝尔·斯蒂格伍德称,从“绝望”到“乐观”,试验让她重燃希望。另一位参与者汉娜·斯雷尔福尔也表示:“结果令人振奋,相信治愈将成为现实。”
多发性硬化症协会研究主任艾玛·格雷博士指出,这是数十年研究的突破:“这些药物或成治疗转折点,为修复髓鞘带来真正希望。”但该机构提醒,仍需进一步研究才能获批应用。
Edited by Kun Liang
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